Found 25 matching trials
Long-Term Follow Up Study of Subjects Previously Administered HMI 102
N/AAn Open-Label, Long-Term Follow Up Study of Safety and Efficacy in PKU Subj...
Status
Enrolling By Invitation
Location
Boston Children's Hospital
Liver Cell Transplant for Phenylketonuria
PHASE1Human phenylketonuria (PKU) results from phenylalanine hydroxylase (PAH) de...
Location
UPMC Children's Hospital of Pittsburgh
Long-Term Extension of Previous rAvPAL-PEG Protocols in Subjects With PKU (PAL-003)
PHASE2This study is an extension of previous rAvPAL-PEG studies. Administration o...
Location
The Children's Hospital
Evaluation of PKU UP
NAPKU UP is a prospective, single-arm, open-label, 26-week acceptability stud...
Location
Royal Belfast Hospital for Sick Children
Efficacy and Safety of Orally Administered Engineered Probiotics (CBT102-A) for the Treatment of Children With Phenylketonuria
EARLY_PHASE1This is a randomized, double-blind, placebo-controlled, parallel-group stud...
Location
Children's Hospital of Fudan University
PKU Skin Stripping
N/APURPOSE OF STUDY: To determine if a non-invasive skin stripping technique c...
Location
Cincinnati Children's Hospital Medical Center
The Effectiveness of Kuvan in Amish PKU Patients
PHASE4The purpose of this study is to determine if Amish patients with PKU show r...
Location
University Hospitals Cleveland Medical Center
Study of Phenoptin in Subjects With Phenylketonuria Who Participated in Protocols PKU-004 or PKU-006
PHASE3The objective of this study is to evaluate the safety of long-term treatmen...
Location
Multiple Locations
A Study to Evaluate Subcutaneously Administered rAvPAL-PEG in Patients With Phenylketonuria for 24 Weeks
PHASE2The primary objective of the study is to evaluate the effect of dosing regi...
Location
The Children's Hospital
A Dose-finding Study to Evaluate mRNA-3210 in Participants With Phenylketonuria
PHASE1The main goal of this study is to assess the safety, and tolerability of mu...
Location
Multiple Locations